WebbKeith Bedford/The Boston Globe. A n experimental hemophilia drug developed by Alnylam Pharmaceuticals continues to staunch bleeding in patients followed for almost one year … WebbBioMarin focuses on treatments for rare diseases. I’m the regional medical lead for PKU and Haemophilia in APAC supporting my colleagues in Australia, Japan, China, Taiwan, South Korea, and the rest of south east Asia. I also sit on BioMarin’s Field Medical Working group focusing on the development and implementation of our Insights collection and …
Rebounding from setbacks, Sanofi reveals promising data for …
WebbSanofi SA said the U.S. Food and Drug Administration has approved its Altuviiio drug, a once weekly treatment for hemophilia A. The French pharmaceutical company SAN, … WebbSanofi’s extended half-life factor replacement therapies for people with hemophilia A and B were launched in 2014, becoming the first innovations in hemophilia management in 20 years. Since then, they have been used to treat over 3,500 people with hemophilia … affinchè accento
Sanofi eyes 2024 filing for haemophilia drug fitusiran, despite …
WebbChesnot/Getty Images. Sanofi and partner Swedish Orphan Biovitrum AB shared positive topline results from their ongoing Phase III trial on a candidate drug for patients … Webb7 feb. 2024 · Enjaymo is the first new drug to emerge from Sanofi's $11 billion acquisition of Bioverativ, a blood disease company spun out of Biogen in 2024. A second experimental drug from that transaction, a long-lasting hemophilia treatment called efanesoctocog alfa, is currently in advanced clinical testing. Webb12 dec. 2024 · New York, NY, and Brisbane, California – December 12, 2024 – Pfizer Inc. (NYSE: PFE) and Sangamo Therapeutics, Inc. (Nasdaq: SGMO), a genomic medicines company, today announced updated follow-up data from the Phase 1/2 Alta study of giroctocogene fitelparvovec, an investigational gene therapy for patients with … kyocera スマホ